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Three basic types of Down Syndrome:
1.  Trisomy 21 - 94% of children with DS (an extra 21st Chromosome)
2.  Translocation - 4% of children with DS (a chromosomal rearrangement usually between chromosome #14 and #21.)
3.  Mosaicism - A mixture of the two separate cell lines in all of the tissues and organs of the body.  Mosaicism occurs after conception.  Not easily recognizable after birth.  May not diagnose until the child is many years old.

General Information on Down Syndrome




              Incidence of Down Syndrome
                 Down syndrome affects people of all ages, races and
                 economic levels. It is the most frequently occurring
                 chromosomal abnormality, occurring once in approximately
                 every 800 to 1,000 live births. Over 350,000 people in the
                 United States alone have Down syndrome.


                When was Down syndrome discovered?
                 For centuries, people with Down syndrome have been alluded
                 to in art, literature and science. It wasn't until the late 19th
                 century, however, that John Langdon Down, an English
                 physician, published an accurate description of a person with
                 Down syndrome. It was this scholarly work, published in 1866,
                 which earned Down the recognition as the "father" of the
                 syndrome. Although other people had previously recognized
                 the characteristics of  the syndrome, it was Down who
                 described the condition as a distinct and separate entity.

                 Throughout the 20th century, advances in medicine and
                 science enabled researchers to investigate the characteristics
                 of people with Down syndrome. In 1959, the French physician,
                 Jerome Lejeune, identified Down syndrome as a
                 chromosomal  anomaly. Instead of the usual 46 chromosomes
                 present in each cell, Lejeune observed 47 in the cells of
                 individuals with Down syndrome. It was later determined that
                 an extra partial or complete 21st chromosome results in the
                 characteristics associated with Down syndrome.


                Why is Down syndrome referred to as  a "genetic
               condition"?
                 The human body is made of cells; all cells contain a center,
                 called a nucleus, in which genetic material is stored. This
                 genetic material, known as genes, carries the codes
                 responsible for all our inherited characteristics.

                 Genes are grouped along rod-like structures called
                 chromosomes. Normally, the nucleus of each cell contains 23
                 pairs of chromosomes, half of which are inherited from each
                 parent.

                 In Down syndrome, however, the cells usually contain not 46,
                 but 47 chromosomes; with the extra chromosome being  a
                 number 21. This excess genetic material, in the form of
                 additional genes along the 21st chromosome, results in Down
                 syndrome.

                 Because 95 percent of all cases of Down syndrome occur
                 because there are three copies of the 21st chromosome, it is
                 referred to as "trisomy 21."

                 Chromosomes may be studied by examining blood or tissue
                 cells. Individual chromosomes are identified, stained and
                 numbered from largest to smallest. The visual display of the
                 chromosomes is known as a karyotype.


                What causes Down syndrome?
                 Down syndrome is usually caused by an error in cell division
                 called non-disjunction. However, two other types  of
                 chromosomal abnormalities, mosaicism and translocation, are
                 also implicated in Down syndrome – although to a much lesser
                 extent. Regardless of the type of Down syndrome which a
                 person may have, all people with Down syndrome have an
                 extra, critical portion of the number 21 chromosome present in
                 all, or some, of their cells. This additional genetic material
                 alters the course of development and causes the
                 characteristics associated with the syndrome.

                 Nondisjunction is a faulty cell division which results in an
                 embryo with three number 21 chromosomes instead of  two.
                 Prior to, or at, conception, a pair of number 21 chromosomes,
                 in either the sperm or the egg, fail to separate.  As the embryo
                 develops, the extra chromosome is replicated in every cell of
                 the body. This faulty cell division is responsible for 95 percent
                 of all cases of Down syndrome.

                 Why nondisjunction occurs is currently unknown, although it
                 does seem to be related to advancing maternal age. Many
                 people are surprised to find out that 80 percent of children
                 born with Down syndrome are born to women under 35 years
                 of age. This is because younger women have higher fertility
                 rates. It does not contradict the fact that  the incidence of births
                 of children with Down syndrome increases with the age of the
                 mother.

                 Although nondisjunction can be of paternal origin, this occurs
                 less frequently. Because this error in cell division is often
                 present in the egg prior to conception, and women are born
                 with their complete store of eggs, it has been postulated that
                 some environmental factors may be implicated in
                 nondisjunction. However, despite years of research, the cause
                 (or causes) of nondisjunction, is still unknown. There seems to
                 be no connection between any type of  Down syndrome and
                 parents' activities before or during pregnancy.

                 Mosaicism occurs when nondisjunction of the 21st
                 chromosome takes place in one of the initial cell divisions
                 after  fertilization. When this occurs, there is a mixture of two
                 types of cells, some containing 46 chromosomes and some
                 containing 47. Those cells with 47 chromosomes contain an
                 extra 21st chromosome. Because of the "mosaic" pattern of
                 the cells, the term mosaicism is used. Mosaicism is rare,
                 being responsible for only one to two percent of all cases of
                 Down syndrome.

                 Some research has shown that individuals with mosaic Down
                 syndrome are less affected than those with trisomy 21;
                 however, broad generalizations are not possible due to the
                 wide range of abilities that people with Down syndrome
                 possess.

                 Translocation is a different type of chromosomal problem and
                 occurs in only three to four percent of people with Down
                 syndrome. Translocation occurs when part of the number 21
                 chromosome breaks off during cell division and attaches to
                 another chromosome. While the total number of chromosomes
                 in the cells remains 46, the presence of an extra part of the
                 number 21 chromosome causes the features of Down
                 syndrome. As with nondisjunction trisomy 21, translocation
                 occurs either prior to or at conception.

                 Unlike nondisjunction, maternal age is not linked to the risk of
                 translocation. Most cases are sporadic, chance events.
                 However, in about one-third of cases, one parent is a carrier of
                 a translocated chromosome. For this reason, the risk of
                 recurrence for translocation is higher than that of
                 nondisjunction. Genetic counseling can be sought  to
                 determine the origin of the translocation.


                What is the chance of having a second child with Down
               syndrome?
                 In general, it is estimated that the risk of having a second child
                 with trisomy 21 or mosaic Down syndrome is about 1 in 100.
                 The risk is higher if one parent is a carrier of a translocated
                 cell.


                Are any prenatal tests available to detect Down
              syndrome?
                 Yes. There are two types of procedures available to pregnant
                 women: screening tests and diagnostic tests. Screening  tests
                 estimate the risk of the fetus having Down syndrome;
                 diagnostic tests tell whether or not the fetus actually has the
                 condition.

                 The most commonly used screening tests are the Triple
                 Screen and the Alpha-fetoprotein Plus. These tests measure
                 quantities of various substances in the blood
                 (alpha-fetoprotein, human chorionic gonadotropin and
                 unconjugated  estriol) and together with the woman's age,
                 estimate her risk of having a child with Down syndrome. These
                 screening tests are typically offered between fifteen and twenty
                 weeks of gestation.

                 Screening tests are of limited value and are often performed in
                 conjunction with a detailed sonogram. These tests  are only
                 able to accurately detect about sixty percent of fetuses with
                 Down syndrome. Many women who undergo these  tests will
                 be given false-positive readings, and some women will be
                 given false-negative readings.

                 The procedures available for prenatal diagnosis of Down
                 syndrome are chorionic villus sampling (CVS), amniocentesis
                 and percutaneous umbilical blood sampling (PUBS). Each one
                 of these procedures carries a small risk of miscarriage as
                 tissue is extracted from the placenta or the umbilical cord to
                 examine the fetus' chromosomes. The procedures are about
                 98 to 99 percent accurate in the detection of Down syndrome.
                 Amniocentesis is usually performed between 12 and 20 weeks
                 of gestation, CVS between eight and 12 weeks and PUBS
                 after 20 weeks.


                How is Down syndrome diagnosed in a newborn?
                 The diagnosis of Down syndrome is usually suspected after
                 birth as a result of the baby's appearance. It is a particularly
                 difficult time, coupled with the natural stresses of childbirth.
                 Although there is no easy way to be informed, most families
                 agree that having the baby present, being together and being
                 told as soon as possible is the best  way to proceed.

                 There are many physical characteristics which form the basis
                 for suspecting an infant has Down syndrome. Many of  these
                 characteristics are found, to some extent, in the general
                 population of individuals who do not have Down syndrome.
                 Hence, if Down syndrome is suspected, a karyotype will be
                 performed to ascertain the diagnosis. Some infants with Down
                 syndrome have only a few of these traits, while others have
                 many. Among the most common traits are:

                     Muscle hypotonia, low muscle tone
                     Flat facial profile, a somewhat depressed nasal bridge
                     and a small nose
                     Oblique palpebral fissures, an upward slant to the eyes
                     Dysplastic ear, an abnormal shape of the ear
                     A single deep crease across the center of the palm
                     Hyperflexibility, an excessive ability to extend the joints
                     Dysplastic middle phalanx of the fifth finger, fifth finger
                     has one flexion furrow instead of two
                     Epicanthal folds, small skin folds on the inner corner of
                     the eyes
                     Excessive space between large and second toe
                     Enlargement of tongue in relationship to size of mouth

              Do babies with Down syndrome have medical
              problems?
                 Children with Down syndrome are at increased risk for certain
                 health problems. Congenital heart defects, increased
                 susceptibility to infection, respiratory problems, obstructed
                 digestive tracts and childhood leukemia occur with greater
                 frequency among children who have Down syndrome.
                 However, advances in medicine have rendered most of these
                 health problems treatable and the majority of people born with
                 Down syndrome today have a life expectancy of approximately
                 55 years.

                 Adults with Down syndrome are at increased risk for
                 Alzheimer's disease. Whereas approximately six percent of
                 the general  population will develop the disease, the figure is
                 about 25 percent for people with Down syndrome. Many
                 individuals with  Down syndrome have the changes in the brain
                 associated with Alzheimer's, but do not necessarily develop
                 the clinical  disorder.
 
 

                How does Down syndrome affect a person's
              development?
                 Most people with Down syndrome have some level of mental
                 retardation; however, the level usually falls into the  mild to
                 moderate range and is not indicative of the many strengths
                 and talents that each individual possesses. Children with
                 Down syndrome learn to sit, walk, talk, play, toilet train and do
                 most other activities – only somewhat  later than their peers
                 without Down syndrome. Because speech is often delayed,
                 careful attention should be paid to the child's hearing, as
                 retention of fluid in the inner ear is a very common cause of
                 hearing and speech difficulties.

                 Early intervention services, which begin shortly after birth, help
                 children with Down syndrome develop to their  full potential.
                 Quality educational programs, along with a stimulating home
                 environment and good medical care enable people with Down
                 syndrome to become contributing members of their families
                 and communities.

                 People with Down syndrome are highly responsive to their
                 physical and social environment. Those who receive good
                 medical care and are included in the activities of the
                 community can be expected to adapt successfully – to attend
                 school, make friends, find work, participate in decisions which
                 affect them and make a positive contribution to society.

                 People with Down syndrome have the same emotions and
                 needs as their peers and deserve the same opportunities.
 
 

                What does the future hold for people  with Down
               syndrome?
                 People with Down syndrome are people first. They may  have
                 some of the characteristics generally associated with this
                 condition, but they are overwhelmingly unique and must be
                 treated as individuals. Over the past few decades, beginning
                 with Section 504 of The Rehabilitation Act of 1973, continuing
                 with The Education for All Handicapped Children Act of 1975
                 and culminating with the passage of the Americans with
                 Disabilities Act in 1991, people with Down syndrome have
                 been granted equal protections under federal law.

                 Ensuring equal treatment and access to services is a struggle
                 that every family of a child with Down syndrome faces. Daily,
                 these individuals strive to accomplish the same goals as
                 everyone else: self-fulfillment, pride in their achievements,
                 inclusion in the activities of the community and the challenge of
                 reaching their full potential.

                 Daily, people with Down syndrome venture out into the
                 community: to schools, jobs and leisure activities. Some live
                 with family, some with friends and some independently. They
                 form ongoing interpersonal relationships and some may marry.
                 Women with Down syndrome are fertile and can have children.

                 The opportunities available to people with Down syndrome
                 today have never been greater. However, it is only through the
                 collective efforts of parents, professionals and concerned
                 citizens that acceptance is becoming widespread. It is the goal
                 of the National Down Syndrome Society to ensure that all
                 people with Down syndrome are provided  the opportunity to
                 achieve their full potential in all aspects of community life.

Questions & Answers

              Why should we be concerned about Down syndrome?
                 Chromosomal abnormalities are a widespread medical
                 problem, with Down syndrome being the most common
                 genetic condition. One in every 800 to 1,000 children is born
                 with Down syndrome.

                 More than 50 percent of miscarriages are caused by a
                 chromosomal abnormality. As many as 25 percent of all
                 miscarriages are caused by a trisomy, which is the presence
                 of three copies of a particular chromosome, rather than the
                 normal two.

                 The most common form of Down syndrome is called Trisomy
                 21, because it involves an extra copy of the 21st chromosome.
                 Twenty to 25 percent of children conceived with Down
                 syndrome survive past birth.
 
 

                What impact does Down syndrome have on society?
                 Individuals with Down syndrome are becoming increasingly
                 integrated into society and community organizations, such as
                 school, health care systems, work forces and social and
                 recreational activities. Individuals with Down syndrome
                 possess varying degrees of mental retardation, from very mild
                 to severe. Most people with Down syndrome have IQs in the
                 mild to moderate range of mental retardation.

                 Due to advances in medical technology, individuals with Down
                 syndrome are living longer than ever before. In 1910, children
                 with Down syndrome were expected to survive to age nine.
                 With the discovery of antibiotics, the average survival age
                 increased to 19 or 20. Now, with recent advancements in
                 clinical treatment, as many as 80 percent of adults with Down
                 syndrome reach age 55, and many live even longer.

                 In the United States, approximately 350,000 families are
                 affected by Down syndrome. Approximately 5,000 children
                 with Down syndrome are born each year. As the mortality rate
                 associated with Down syndrome is decreasing, the
                 prevalence  of individuals with Down syndrome in our society
                 will increase. Some experts project that the number of people
                 with Down syndrome will double in the next 10 years. More and
                 more Americans will interact with individuals with  this genetic
                 condition, increasing the need for widespread public
                 education and acceptance.
 
 

                Is Down syndrome transmitted from  the mother or
              father?
                 The additional genetic material which causes Down syndrome
                 can originate from either the father or the mother.
                 Approximately five percent of the cases have been traced to
                 the father.
 
 

                Who has the highest risk of having a child with Down
              syndrome?
                 Down syndrome affects people of all races and economic
                 levels. Women age 35 and older have a significantly increased
                 risk of having a child with Down syndrome. A 35-year-old
                 woman has a one in 400 chance of conceiving a child with
                 Down syndrome and this chance increases gradually to one in
                 110 by age 40. At age 45 the incidence becomes
                 approximately one in 35.

                 Since many couples are postponing parenting until later in life,
                 the incidence of Down syndrome conceptions is  expected to
                 increase. Therefore, genetic counseling for parents is
                 becoming increasingly important. Still, many physicians are not
                 fully informed about advising their patients about the of
                 incidence of Down syndrome, advancements in diagnosis and
                 the protocols for care and treatment of babies born with Down
                 syndrome.
 
 

                Why is it important to raise children  with Down
               syndrome at home?
                 A greater understanding of Down syndrome and
                 advancements in treatment of Down syndrome-related health
                 problems have allowed people with Down syndrome to enjoy
                 fuller and more active lives.

                 Children raised at home and included in all aspects of
                 community life can best reach their potential and function  in
                 society with a greater degree of independence. Parental love,
                 nurturing and support, as well as early intervention programs,
                 educational opportunities and community involvement, have a
                 direct relationship to the degree that a person with Down
                 syndrome is able to achieve his/her potential.
 
 

                Why are medical researchers following Down syndrome
              work so closely?
                 Down syndrome is a developmental disorder. As researchers
                 learn more about the molecular genetics and other aspects of
                 Down syndrome, they also obtain valuable information about
                 human development and can advance the study of many
                 biological processes.

                 In addition, individuals with Down syndrome have a higher
                 incidence of certain medical problems and the study of Down
                 syndrome may yield important breakthroughs in those areas.
                 Research in Down syndrome provides a way for looking at
                 many important problems:

                     Heart disease: Up to 50 percent of individuals with
                     Down syndrome are born  with congenital heart defects.
                     The majority of heart defects in children with Down
                     syndrome can now be surgically corrected with resulting
                     long-term health improvements. However, scientists
                     continue to search for the cause of  this problem and
                     look for means of prevention.

                     Alzheimer's disease: Estimates vary, but it is
                     reasonable to conclude that 25 percent or more of
                     individuals with Down syndrome over the age of 35 will
                     develop the clinical signs and symptoms of
                     Alzheimer's-type dementia.

                     Leukemia: Individuals with Down syndrome have a 15 to
                     20 times greater risk of developing leukemia. The
                     majority of cases are categorized as acute
                     megakaryoblastic leukemia, which tends to occur in the
                     first three years of life, and for which there is a high cure
                     rate. A transient form of leukemia is also seen in
                     newborns with Down syndrome, disappearing
                     spontaneously during the first two to three months of life.
 
 

                Why hasn't Down syndrome received much attention in
               the past?
                 Even though Dr. Jerome Lejeune discovered in 1959 that it
                 was an extra 21st chromosome that caused Down syndrome,
                 it is only in the last few years that a focus has been placed on
                 the study of the 21st chromosome.

                 In May 2000, researchers completed sequencing the
                 approximately 225 genes on the 21st chromosome - only the
                 second chromosome to be fully sequenced at this time.
                 Although these findings will not have an immediate impact on
                 the Down syndrome community, they will open the door to
                 valuable research on this small set of genes.

                 Researchers continue to look for the genes related to the
                 development of intelligence and the physical characteristics
                 associated with Down syndrome. Once identified, it is hoped
                 that the biochemical process which causes Down syndrome
                 can be decoded, leading to the development of an intervention
                 and cure. See the Research section of this Web site for more
                 information about sequencing the 21st chromosome.
 
 

                What is the National Down Syndrome  Society doing to
               further research?
                 NDSS is currently sponsoring three scientists through the
                 NDSS Science Scholar Award Program initiated in 1983.
                 Under this grant program, each researcher receives $35,000 a
                 year for two years to carry out scientific research into the
                 causes and/or amelioration of Down syndrome. To date, more
                 than 20 scholars have been supported by this program.

                 NDSS also sponsors a series of annual symposia focusing on
                 Down syndrome research. This sharing of information,
                 technology and the collective knowledge of the world's
                 foremost researchers is expected to produce an acceleration
                 of advancements in a variety of areas. The proceedings of
                 these scientific symposia are published annually and are
                 available through NDSS.
 
 

Myths and Truths
 

Myth: Down syndrome is a rare genetic disorder.

                 Truth: Down syndrome is the most commonly occurring
                 genetic condition. One in every 800 to 1,000 live births is a
                 child  with Down syndrome, representing approximately 5,000
                 births per year in the United States alone. Today, Down
                 syndrome affects more than 350,000 people in the United
                 States.

                 Myth: Most children with Down syndrome are born to
                 older parents.

                 Truth: Eighty percent of children born with Down syndrome
                 are born to women younger than 35-years-old. However, the
                 incidence of births of children with Down syndrome increases
                 with the age of the mother.

                Myth: People with Down syndrome are severely
                 retarded.

                 Truth: Most people with Down syndrome have IQs that fall in
                 the mild to moderate range of retardation. Children with Down
                 syndrome are definitely educable and educators and
                 researchers are still discovering the full educational potential of
                 people with Down syndrome.

                Myth: Most people with Down syndrome are
                 institutionalized.

                 Truth: Today people with Down syndrome live at home with
                 their families and are active participants in the educational,
                 vocational, social and recreational activities of the community.
                 They are integrated into the regular education system, and
                 take part in sports, camping, music, art programs and all the
                 other activities of their communities. In addition, they are
                 socializing with people with and without disabilities, and as
                 adults are obtaining employment and living in group homes
                 and other independent housing arrangements.

                Myth: Parents will not find community support in
                 bringing up their child with Down syndrome.

                 Truth: In almost every community of the United States there
                 are parent support groups and other community organizations
                 directly involved in providing services to families of individuals
                 with Down syndrome.

                Myth: Children with Down syndrome must be placed in
                 segregated special education programs.

                 Truth: Children with Down syndrome have been included in
                 regular academic classrooms in schools across the country. In
                 some instances they are integrated into specific courses, while
                 in other situations students are fully included in the regular
                 classroom for all subjects. The degree of mainstreaming is
                 based in the abilities of the individual; but the trend is for full
                 inclusion in the social and educational life of the community.

                Myth: Adults with Down syndrome are unemployable.

                 Truth: Businesses are seeking young adults with Down
                 syndrome for a variety of positions. They are being employed
                 in small and medium sized offices: by banks, corporations,
                 nursing homes, hotels and restaurants. They work in the music
                 and entertainment industry, in clerical positions and in the
                 computer industry. People with Down syndrome bring to their
                 jobs enthusiasm, reliability and dedication.

                Myth: People with Down syndrome are always happy.

                 Truth: People with Down syndrome have feelings just like
                 everyone else in the population. They respond to positive
                 expressions of friendship and they are hurt and upset by
                 inconsiderate behavior.

                 Myth: Adults with Down syndrome are unable to form
                 close interpersonal relationships leading to marriage.

                 Truth: People with Down syndrome date, socialize and form
                 ongoing relationships. Some are beginning to marry. Women
                 with Down syndrome can and do have children, but there is a
                 50 percent chance that their child will have Down syndrome.
                 Men with Down syndrome are believed to be sterile, with only
                 one documented instance of a male with Down syndrome who
                 has fathered a child.

                 Myth: Down syndrome can never be cured.

                 Truth: Research on Down syndrome is making great strides
                 in identifying the genes on chromosome 21 that cause the
                 characteristics  of Down syndrome. Scientists now feel
                 strongly that it will be possible to improve, correct or prevent
                 many of  the problems associated with Down syndrome in the
                 future.




Limited Funding Available for Children with Medical Needs
The Disabled Children's Relief Fund (DCRF) is a small, private foundation, has some funding for medical expenses for children with disabilities such as DS.  DCRF focuses special attention on helping children that do not have health insurance, especialy children with disabilities.  To learn more about the fund contact:  DCRF, 402 Pennsylvania Avenue, Freeport, NY.  11520 or phone: (516) 377-1605 or Fax:  (516) 377-3978.


E-MAIL  at: robeng@ix.netcom.com

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